Repositioning 'old' drugs to treat rare diseases: arguing from the mechanism of action

Marjolein Drent, Aalt Bast, Hans Peter Bootsma, Vera Deneer

Research output: Contribution to journalArticleAcademicpeer-review

Original languageEnglish
Pages (from-to)191-194
Number of pages4
JournalSarcoidosis, vasculitis, and diffuse lung diseases : official journal of WASOG
Volume33
Issue number2
Publication statusPublished - 1 Aug 2016

Keywords

  • histiocytosis-X, orphan drugs, pharmacological treatment, rare disease

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