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CRISPR-Cas9 gene editing: Delivery aspects and therapeutic potential
Erik Oude Blenke
, Martijn J W Evers
,
Enrico Mastrobattista
, John van der Oost
*
*
Corresponding author for this work
UIPS - Utrecht Institute for Pharmaceutical Sciences
Pharmaceutics
Utrecht University
Wageningen University & Research
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Keyphrases
Therapeutic Potential
100%
Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR)
100%
Cas9 Protein
100%
Gene Editing
100%
Clustered Regularly Interspaced Short Palindromic repeats/Cas9
100%
Editing System
50%
Anti-CRISPR Proteins
50%
Mammalian Cells
25%
Associated Proteins
25%
Adaptive Immune Response
25%
Protein-coding Genes
25%
Scientific Impact
25%
Human Body
25%
Human Patients
25%
Current Form
25%
Nobel Prize
25%
Genetic mutation
25%
Genetic Disease
25%
Biomedical Science
25%
Therapeutic Modalities
25%
Protein System
25%
Off-target Effects
25%
Genome Editing
25%
Repurposing
25%
Delivery Technologies
25%
Patent Wars
25%
In Vivo Applications
25%
Medicine and Dentistry
Clustered Regularly Interspaced Short Palindromic Repeat
100%
Cas9
100%
CRISPR Associated Protein
50%
Gene Mutation
16%
Adaptive Immunity
16%
Biomedical Discipline
16%
Genetic Disorder
16%
Mammalian Cell
16%
Therapeutic Modality
16%
Genome Editing
16%
Neuroscience
CRISPR
100%
CRISPR Associated Protein
50%
In Vivo
16%
Gene Mutation
16%
Pharmacology, Toxicology and Pharmaceutical Science
CRISPR Associated Protein
100%
Genetic Disorder
33%